A longitudinal study of the relationship between impairment, activity limitation, participation and quality of life in persons with confirmed Duchenne Muscular Dystrophy
Long-term assessment of people with Duchenne muscular dystrophy
The purpose of this study is to establish the largest long-term assessment of people with Duchenne muscular dystrophy (DMD) by looking at how long-term steroid therapy affects the lives of children who use the drug. A second purpose of this study is to find out whether small differences in the genetic makeup of people with DMD affect how their disease progresses and how they respond to steroids.
Participate in this study
Who can participate
Recruitment has closed.
Interested in participating
If you have questions about the study, please contact Gloria Lee at 416.425.6220 ext. 3342 with your interest, and she will get back to your shortly.
U.S. Department of Education, National Institutes of Health, U.S. Department of Defense and Parent Project Muscular Dystrophy